Drug Type AAV based gene therapy |
Synonyms gene therapy (Oxford University) |
Target |
Mechanism UTRN activators(Utrophin activators), dystrophin modulators(Dystrophin modulators) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Muscular Dystrophy, Duchenne | Discovery | GB | - |