Drug Type Gene editing |
Synonyms LNP-delivered CRISPR gene-editing therapy(Acuitas Therapeutics), mRNA+RNA+ALC-0307+ALC-0159 therapy(Acuitas Therapeutics) |
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Action- |
Mechanism- |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
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Drug Highest PhaseClinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
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Urea Cycle Disorders, Inborn | Clinical | - | - |