Drug Type Chemical drugs |
Synonyms DM1 (TransitionBio) |
Target |
Mechanism DMPK modulators(DM1 protein kinase modulators), MBNL1 modulators(muscleblind like splicing regulator 1 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization ![]() |
Active Organization ![]() |
Inactive Organization- |
Drug Highest PhaseDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Myotonic Dystrophy | Discovery | US | ![]() | 01 Nov 2024 |