Drug Type AAV based gene therapy |
Synonyms AB0-201 |
Target |
Mechanism CLN3 modulators(Battenin modulators) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingPreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Neuronal Ceroid-Lipofuscinoses | Preclinical | US | 01 Jan 2021 |