Drug Type ASO |
Synonyms Targeting TUBB4A ASO (SynaptixBio), SB 19642, SB19642 |
Target |
Action inhibitors |
Mechanism TUBB4A inhibitors(tubulin beta 4A class IVa inhibitors) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePhase 1 |
First Approval Date- |
RegulationOrphan Drug (United States) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Leukodystrophy, Hypomyelinating, 6 | Phase 1 | United Kingdom | 11 Jun 2025 |