Last update 13 Dec 2025

Retinitis Pigmentosa/Usher Syndrome (Prime Medicine)

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
USH2A gene therapy(Prime Medicine), Usher Syndrome gene editing therapy (Prime Medicine)
Target
usherin
Action
modulators
Mechanism
usherin modulators(Usherin modulators)
Therapeutic Areas
Congenital DisordersEye DiseasesOther Diseases+ [2]
Active Indication-
Inactive Indication
Retinitis PigmentosaUsher Syndromes
Originator Organization
Prime Medicine, Inc.Prime Medicine, Inc.
Active Organization-
Inactive Organization
Prime Medicine, Inc.Prime Medicine, Inc.
License Organization-
Drug Highest PhaseDiscontinuedPreclinical
First Approval Date-
Regulation-

Related

100 Clinical Results associated with Retinitis Pigmentosa/Usher Syndrome (Prime Medicine)
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100 Translational Medicine associated with Retinitis Pigmentosa/Usher Syndrome (Prime Medicine)
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100 Patents (Medical) associated with Retinitis Pigmentosa/Usher Syndrome (Prime Medicine)
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100 Deals associated with Retinitis Pigmentosa/Usher Syndrome (Prime Medicine)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Retinitis PigmentosaPreclinical
United States
Prime Medicine, Inc.Prime Medicine, Inc.
01 Oct 2024
Usher SyndromesDiscovery
United States
Prime Medicine, Inc.Prime Medicine, Inc.
07 Sep 2023
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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