Drug Type AAV based gene therapy |
Synonyms AAV-RCas13d (Locana), C9ORF72-FTD |
Target |
Action modulators |
Mechanism C9orf72 gene modulators |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhaseDiscovery |
First Approval Date- |
Regulation- |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Pick Disease of the Brain | Discovery | United States | - |





