Drug Type AAV based gene therapy |
Synonyms- |
Target |
Mechanism AGL modulators(amylo-alpha-1, 6-glucosidase, 4-alpha-glucanotransferase modulators) |
Active Indication- |
Inactive Indication |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Glycogen Storage Disease Type III | Preclinical | FR | - |