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Last update 27 Aug 2025
Mini-GDE gene therapy (Genethon)
Last update 27 Aug 2025
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms AAV based gene therapy (Genethon) |
Target |
Action modulators |
Mechanism AGL modulators(amylo-alpha-1, 6-glucosidase, 4-alpha-glucanotransferase modulators) |
Active Indication |
Inactive Indication- |
R&D Status
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Glycogen Storage Disease Type III | Preclinical | France | 16 Jan 2024 |
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Clinical Result
Clinical Result
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