Drug Type Gene therapy |
Synonyms- |
Target |
Action modulators |
Mechanism NPHP1 modulators(nephrocystin 1 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization |
Drug Highest PhaseDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Retinal Dystrophies | Discovery | United States | 05 May 2025 | |
Retinal Dystrophies | Discovery | United States | 05 May 2025 |