Drug Type AAV based gene therapy |
Synonyms adeno-associated viral vector delivered human glucocerebrosidase gene therapy (Royal Free Hospital) |
Target- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Gaucher Disease | Discovery | GB | - |