Drug Type Gene editing |
Synonyms GEN 6044, GEN6044 |
Target |
Action modulators |
Mechanism DMD exon 44 modulators(Dystrophin exon 44 modulators) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhaseDiscontinuedDiscovery |
First Approval Date- |
Regulation- |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Muscular Dystrophy, Duchenne | Discovery | China | 12 Jun 2024 |





