Drug Type Gene therapy |
Synonyms GT CN 100 |
Target |
Mechanism CAPN3 stimulants(Calpain-3 stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Limb-Girdle Muscular Dystrophy Type 2A | Preclinical | RU | 19 Jun 2024 |