Drug Type AAV based gene therapy, Gene editing |
Synonyms- |
Target |
Mechanism ATXN2 gene modulators |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Amyotrophic Lateral Sclerosis | Preclinical | CN | 08 May 2024 |