Drug Type Gene therapy |
Synonyms TALEN®-edited CD34+ HSC gene therapy |
Target |
Mechanism β-globin modulators(Hemoglobin beta chain modulators) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingPreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Anemia, Sickle Cell | Preclinical | US | 15 Dec 2021 |