Drug Type AAV based gene therapy |
Synonyms myotubularin gene-encoding AAV 8 vector based therapy (Genethon/ Wake Forest University/University of Washington/Harvard Medical School/INSERM) |
Target- |
Action- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Muscular Diseases | Preclinical | France | - |