Last update 30 Aug 2025

Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene(Genethon)

Overview

Basic Info

Drug Type
Cell therapy
Synonyms-
Target
CD34
Action
modulators
Mechanism
CD34 modulators(Hematopoietic progenitor cell antigen CD34 modulators)
Therapeutic Areas
Immune System DiseasesCongenital DisordersHemic and Lymphatic Diseases+ [1]
Active Indication-
Inactive Indication
Wiskott-Aldrich Syndrome
Originator Organization
GenethonGenethon
Active Organization-
Inactive Organization
GenethonGenethon
License Organization-
Drug Highest PhasePendingPhase 1/2
First Approval Date-
Regulation-
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Related

2
Clinical Trials associated with Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene(Genethon)
NCT01347346
/ CompletedPhase 1/2IIT
Phase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott-Aldrich Syndrome
NCT01347242
/ CompletedPhase 1/2IIT
Phase I/II Clinical Trial of Haematopoietic Stem Cell Gene Therapy for the Wiskott-Aldrich Syndrome
100 Clinical Results associated with Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene(Genethon)
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100 Translational Medicine associated with Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene(Genethon)
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100 Patents (Medical) associated with Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene(Genethon)
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100 Deals associated with Autologous CD34 positive cells transduced with a lentiviral vector containing human WAS gene(Genethon)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Wiskott-Aldrich SyndromePhase 2
United Kingdom
GenethonGenethon
01 Mar 2011
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Clinical Result

Indication
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Clinical Trial

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Approval

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Regulation

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