Drug Type AAV based gene therapy |
Synonyms Biostrophin, Muscular dystrophy gene therapy, rAAV2.5-CMV-minidystrophin (d3990) |
Target |
Mechanism mini-dystrophin stimulants(mini-dystrophin stimulants) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingPhase 1 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Muscular Dystrophy, Duchenne | Phase 1 | - | - |