Drug Type AAV based gene therapy |
Synonyms |
Target |
Mechanism RLBP1 stimulants(retinaldehyde binding protein 1 stimulants) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization ![]() |
Drug Highest PhasePendingPreclinical |
First Approval Date- |
RegulationOrphan Drug (EU) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Retinitis punctata albescens | Preclinical | FR | ![]() | 11 Jul 2017 |
Retinitis punctata albescens | Preclinical | US | ![]() | 11 Jul 2017 |