Drug Type Gene editing |
Synonyms FMR1 gene therapy (Prime Medicine) |
Target |
Action modulators |
Mechanism FMRP modulators(FMRP translational regulator 1 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhaseDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Fragile X Syndrome | Discovery | United States | 07 Sep 2023 |