Drug Type AAV based gene therapy |
Synonyms AAV9-G6PC1 gene therapy (Genethon), AAV9-based gene therapy (Genethon) |
Target |
Action stimulants |
Mechanism G6PC gene stimulants(Glucose-6-phosphatase gene stimulants) |
Active Indication |
Inactive Indication- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Glycogen Storage Disease | Preclinical | France | - |