Drug Type Gene therapy, Hematopoietic stem cell therapy |
Synonyms OTL 202, OTL202 |
Target |
Action- |
Mechanism NAGLU replacements(Alpha-N-acetylglucosaminidase replacements) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhasePendingPreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Mucopolysaccharidosis III | Preclinical | United Kingdom | 04 Aug 2021 |