Last update 18 Dec 2024

CRISPR-SCD-001

Overview

Basic Info

Drug Type
Hematopoietic stem cell therapy
Synonyms
CRISPR-SCD-001
Target
endonuclease Cas9 x β-globin
Mechanism
HBB gene stimulants(Hemoglobin beta chain gene stimulants), endonuclease Cas9 modulators
Therapeutic Areas
Immune System DiseasesUrogenital Diseases
Active Indication
Kidney Failure, ChronicRenal transplant rejection
Inactive Indication-
Originator Organization
University of California, Los AngelesUniversity of California, Los Angeles
Active Organization
University of California, Los AngelesUniversity of California, Los Angeles
Inactive Organization-
Drug Highest PhasePhase 1
First Approval Date-
Regulation-
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Related

1
Clinical Trials associated with CRISPR-SCD-001
NCT05525507 / RecruitingPhase 1IIT
A Single-armed, Unblinded, Non-randomized Feasibility Study of Hematopoietic Stem Cell Infusion Following a Conditioning Regimen of Total Lymphoid Irradiation (TLI) and Anti-thymocyte Globulin (ATG) in Patients With a Pre-existing, Well-functioning HLA-identical Kidney Transplant
100 Clinical Results associated with CRISPR-SCD-001
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100 Translational Medicine associated with CRISPR-SCD-001
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100 Patents (Medical) associated with CRISPR-SCD-001
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100 Deals associated with CRISPR-SCD-001
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Kidney Failure, ChronicPhase 1
US
University of California, Los AngelesUniversity of California, Los Angeles
21 Dec 2022
Renal transplant rejectionPhase 1
US
University of California, Los AngelesUniversity of California, Los Angeles
21 Dec 2022
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Clinical Result

Indication
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Approval

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Regulation

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