Drug Type Gene therapy |
Synonyms |
Target |
Mechanism DYSF gene stimulants(Dysferlin gene stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Limb-Girdle Muscular Dystrophy, Type 2B | Preclinical | RU | 20 Jun 2024 | |
Myofibrillar Myopathy | Preclinical | RU | 30 Nov 2022 |