Drug Type Gene therapy |
Synonyms GT DF 100 |
Target |
Action stimulants |
Mechanism DYSF gene stimulants(Dysferlin gene stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Limb-Girdle Muscular Dystrophy, Type 2B | Preclinical | Russia | 20 Jun 2024 | |
| Myofibrillar Myopathy | Preclinical | Russia | 30 Nov 2022 |





