Drug Type AAV based gene therapy  | 
Synonyms AAV PAH (Dimension), DTX-501  | 
Target  | 
Action agonists  | 
Mechanism PAH agonists(Phenylalanine hydroxylase agonists)  | 
Therapeutic Areas  | 
Active Indication-  | 
Inactive Indication  | 
Originator Organization  | 
Active Organization-  | 
Inactive Organization  | 
License Organization-  | 
Drug Highest PhasePendingDiscovery  | 
First Approval Date-  | 
Regulation-  | 
| Indication | Highest Phase | Country/Location | Organization | Date | 
|---|---|---|---|---|
| Phenylketonurias | Discovery | United States   | - | 





