Drug Type CRISPR/Cas9 |
Synonyms HCU treatment gene editing therapy (Tome Biosciences) |
Target |
Action modulators |
Mechanism CBS modulators(cystathionine beta-synthase modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhaseDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Homocystinuria | Discovery | United States | 04 Jun 2024 |