Drug Type AAV based gene therapy |
Synonyms Adeno-associated virus (AAV)-based gene replacement therapy for STXBP1-related disorders(Encoded Therapeutics) |
Target |
Action modulators |
Mechanism STXBP1 modulators(syntaxin binding protein 1 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
STXBP1-related epileptic encephalopathy | Preclinical | United States | 07 May 2024 |