Drug Type AAV based gene therapy  | 
Synonyms Adeno-associated virus (AAV)-based gene replacement therapy  for STXBP1-related disorders(Encoded Therapeutics)  | 
Target  | 
Action modulators  | 
Mechanism STXBP1 modulators(syntaxin binding protein 1 modulators)  | 
Therapeutic Areas  | 
Active Indication  | 
Inactive Indication-  | 
Originator Organization  | 
Active Organization  | 
Inactive Organization-  | 
License Organization-  | 
Drug Highest PhasePreclinical  | 
First Approval Date-  | 
Regulation-  | 
| Indication | Highest Phase | Country/Location | Organization | Date | 
|---|---|---|---|---|
| STXBP1-related epileptic encephalopathy | Preclinical | United States   | 07 May 2024 | 





