Drug Type Gene therapy |
Synonyms EPI-111, EPIC-111 |
Target |
Action modulators |
Mechanism PRPF31 modulators(pre-mRNA processing factor 31 modulators) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhaseDiscontinuedDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Retinitis Pigmentosa 11 | Discovery | United States | 15 Aug 2022 |