Drug Type AAV based gene therapy |
Synonyms Aromatic l-amino acid decarboxylase deficiency gene therapy |
Target |
Action- |
Mechanism DDC replacements(DOPA decarboxylase replacements), Gene transference |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1/2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Aromatic Amino Acid Decarboxylase Deficiency | Phase 2 | Japan | 14 Mar 2022 | |
Parkinson Disease | Preclinical | Japan | - |