Last update 05 Jul 2025

gcHBB-SCD

Overview

Basic Info

Drug Type
Gene editing
Synonyms-
Target
β-globin
Action
modulators
Mechanism
β-globin modulators(Hemoglobin beta chain modulators)
Therapeutic Areas
Congenital DisordersHemic and Lymphatic DiseasesOther Diseases
Active Indication-
Inactive Indication
Anemia, Sickle Cell
Originator Organization
Stanford UniversityStanford University
Active Organization-
Inactive Organization
Stanford UniversityStanford University
License Organization-
Drug Highest PhasePendingPreclinical
First Approval Date-
Regulation-

Related

100 Clinical Results associated with gcHBB-SCD
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100 Translational Medicine associated with gcHBB-SCD
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100 Patents (Medical) associated with gcHBB-SCD
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1
Literatures (Medical) associated with gcHBB-SCD
16 Jun 2021Science translational medicineQ1 · MEDICINE
Development of β-globin gene correction in human hematopoietic stem cells as a potential durable treatment for sickle cell disease
Q1 · MEDICINE
100 Deals associated with gcHBB-SCD
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Anemia, Sickle CellPreclinical
United States
Stanford UniversityStanford University
15 Jun 2021
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Clinical Result

Indication
Phase
Evaluation
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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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