Drug Type AAV based gene therapy |
Synonyms- |
Target |
Action modulators |
Mechanism UGT1A1 modulators(UDP-glucuronosyltransferase 1-1 modulators), Gene transference |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
License Organization- |
Drug Highest PhasePendingDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Crigler-Najjar Syndrome | Discovery | Europe | - |