Last update 06 Dec 2025

ANB-004(Biocad)

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
ANB004 Biocad, ANB 004 - Biocad
Target
SMN1
Action
modulators
Mechanism
survival of motor neuron 1, telomeric modulators
Therapeutic Areas
Nervous System DiseasesOther Diseases
Active Indication
HMN (Hereditary Motor Neuropathy) Proximal Type I
Inactive Indication-
Originator Organization
Biocad CJSCBiocad CJSC
Active Organization
Biocad CJSCBiocad CJSC
Inactive Organization-
License Organization-
Drug Highest PhasePhase 1/2
First Approval Date-
Regulation-
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Related

1
Clinical Trials associated with ANB-004(Biocad)
NCT05747261
/ RecruitingPhase 1/2
An Open-Label, Non-Comparative Clinical Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene (ANB-004 (JSC BIOCAD, Russia)) After a Single Intravenous Administration of Escalating Doses in Children With Spinal Muscular Atrophy
100 Clinical Results associated with ANB-004(Biocad)
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100 Translational Medicine associated with ANB-004(Biocad)
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100 Patents (Medical) associated with ANB-004(Biocad)
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100 Deals associated with ANB-004(Biocad)
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R&D Status

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IndicationHighest PhaseCountry/LocationOrganizationDate
HMN (Hereditary Motor Neuropathy) Proximal Type IPhase 2
Belarus
Biocad CJSCBiocad CJSC
02 Feb 2023
HMN (Hereditary Motor Neuropathy) Proximal Type IPhase 2
Russia
Biocad CJSCBiocad CJSC
02 Feb 2023
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Clinical Result

Indication
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Clinical Trial

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Approval

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Regulation

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