Last update 21 Nov 2024
UX-055
Last update 21 Nov 2024
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms AAV9/hCDKL5 (Ultragenyx) + [1] |
Target |
Mechanism CDKL5 stimulants(cyclin dependent kinase like 5 stimulants), Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
R&D Status
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| CDKL5 Deficiency Disorder | Preclinical | US | - | |
| Genetic Diseases, X-Linked | Discovery | US | - |
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Clinical Result
Clinical Result
Indication
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