Drug Type AAV based gene therapy |
Synonyms Wild-type FIX AAVrh10 vector, AAVRH10FIX, DTX 101 + [1] |
Target |
Mechanism Factor IX gene transference, Blood coagulation pathway activation |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhaseDiscontinuedPhase 1/2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Hemophilia B | Phase 2 | US | - | |
Hemophilia B | Phase 2 | BG | - |