Drug Type AAV based gene therapy |
Synonyms AAV-based Angelman syndrome therapy - Sarepta Therapeutics/StrideBio |
Target |
Mechanism UBE3A stimulants(ubiquitin protein ligase E3A stimulants) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization StrideBio, Inc.Startup |
Active Organization StrideBio, Inc.Startup |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Angelman Syndrome | Preclinical | US | StrideBio, Inc.Startup | - |