Last update 17 May 2025

Angelman Syndrome(Sangamo)

Overview

Basic Info

Drug Type
Gene therapy
Synonyms-
Target
UBE3A
Action
modulators
Mechanism
UBE3A modulators(ubiquitin protein ligase E3A modulators), Gene expression modulators
Therapeutic Areas
Nervous System DiseasesCongenital DisordersOther Diseases
Active Indication
Angelman Syndrome
Inactive Indication-
Originator Organization
Sangamo Therapeutics, Inc.Sangamo Therapeutics, Inc.
Active Organization
Sangamo Therapeutics, Inc.Sangamo Therapeutics, Inc.
Inactive Organization-
License Organization-
Drug Highest PhasePreclinical
First Approval Date-
Regulation-

Related

100 Clinical Results associated with Angelman Syndrome(Sangamo)
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100 Translational Medicine associated with Angelman Syndrome(Sangamo)
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100 Patents (Medical) associated with Angelman Syndrome(Sangamo)
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100 Deals associated with Angelman Syndrome(Sangamo)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Angelman SyndromePreclinical
United States
Sangamo Therapeutics, Inc.Sangamo Therapeutics, Inc.
23 Apr 2024
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date

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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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