Drug Type Gene therapy |
Synonyms- |
Target |
Mechanism KCNJ13 gene modulators |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization Spotlight Therapeutics, Inc.Startup |
Active Organization Spotlight Therapeutics, Inc.Startup |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Leber Congenital Amaurosis | Preclinical | US | Spotlight Therapeutics, Inc.Startup | 30 Jun 2024 |