Drug Type AAV based gene therapy |
Synonyms- |
Target- |
Action- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhaseDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Ornithine Carbamoyltransferase Deficiency Disease | Phase 2 | United States | - | |
Polycystic Kidney, Autosomal Dominant | Discovery | United States | - |