Drug Type CRISPR/Cas9 |
Synonyms- |
Target |
Mechanism Ube3a-ATS modulators(small nucleolar RNA host gene 14 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Angelman Syndrome | Preclinical | US | 21 Oct 2020 |