Drug Type AAV based gene therapy |
Synonyms- |
Target |
Action modulators |
Mechanism GUCY2D modulators(guanylate cyclase 2D, retinal modulators), Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingPreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Leber Congenital Amaurosis | Preclinical | Italy | - |