Drug Type Hematopoietic stem cell therapy |
Synonyms gamma-globin reactivated autologous hematopoietic stem cell therapy (BRL Medicine Inc.), HBG gene edited bone marrow-derived CD34-positive autologous HSC therapy (BRL Medicine Inc.), BYC-103 |
Target |
Mechanism HBG gene stimulators |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingPhase 2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Thalassemia | Phase 2 | CN | 21 Jul 2020 |