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Last update 08 May 2025
DMPK CRISPR/Cas9-gene therapy (Genethon)
Last update 08 May 2025
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms- |
Target |
Action modulators |
Mechanism DMPK gene modulators |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
R&D Status
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Myotonic Dystrophy | Preclinical | France | - |
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Clinical Result
Clinical Result
Indication
Phase
Evaluation
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