Drug Type AAV based gene therapy |
Synonyms Adeno-associated vector expressing human codon-optimized arginase 1 under a liver-specific promoter (UCLA Medical Center) |
Target |
Mechanism ARG1 modulators(Arginase-1 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationOrphan Drug (US) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Hyperargininemia | Preclinical | US | 12 Nov 2024 |