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Last update 19 Apr 2025
AGIL FA(PTC Therapeutics, Inc.)
Last update 19 Apr 2025
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms AGIL FA, GT-FA, PTC FA + [1] |
Target |
Action- |
Mechanism Frataxin, mitochondrial replacements, Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhaseDiscontinuedPreclinical |
First Approval Date- |
Regulation- |
R&D Status
10 top R&D records. to view more data
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Friedreich Ataxia | Preclinical | United States | 12 Mar 2016 |
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Clinical Result
Clinical Result
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