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Last update 08 May 2025
EX-054
Last update 08 May 2025
Overview
Basic Info
Drug Type Gene therapy |
Synonyms |
Target- |
Action- |
Mechanism- |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
R&D Status
10 top R&D records. to view more data
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Acidaemia | Preclinical | China | 25 Apr 2024 | |
| Lysosomal Storage Diseases | Preclinical | China | 25 Apr 2024 | |
| Urea Cycle Disorders, Inborn | Preclinical | China | 25 Apr 2024 |
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Clinical Result
Clinical Result
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