Drug Type AAV based gene therapy |
Synonyms gene therapy (Sanofi Genzyme) |
Target |
Action agonists |
Mechanism PAH agonists(Phenylalanine hydroxylase agonists), Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Phenylketonurias | Preclinical | United States | - |