OrphAI Therapeutics Announces Oral Presentation and Posters at the 22nd Annual NEALS Conference
02 Oct 2023
Phase 2Clinical Result
GUILFORD, Conn., Oct. 02, 2023 (GLOBE NEWSWIRE) -- OrphAI Therapeutics Inc., a clinical-stage biopharmaceutical company developing novel therapeutics for rare diseases, announced today data presentations at the 22nd Annual NEALS (Northeast ALS Consortium) meeting being held October 4 - 6, 2023 in Clearwater Florida.
Oral Presentation:
October 5, 2023, 11:10 a.m. ET
Title: Results of the Phase 2a clinical trial of LAM-002A (apilimod dimesylate) in C9orf72 ALS
Presenters: Dr. Suma Babu, Sean M. Healey Center for ALS at MGHl; Peter Young, Ph.D. Chief Scientific Officer, OrphAI Therapeutics.
Location: Opal Ballroom
Poster Presentations:
Title: AIT-101 Improves Functional Deficits in a Human TDP-43 Animal Model of ALS
Presenter: Peter Young, Ph.D., Chief Scientific Officer, OrphAI Therapeutics
Location and Time: Poster Session 1, Abstract:4, October 4, 2023, 5:15p – 7:15p ET
Title: Results of a double blind, placebo-controlled clinical trial of AIT-101 (LAM-002A) in C9ORF72 ALS- A biomarker driven Phase 2a clinical trial targeting PIKfyve inhibition
Presenter: Dr. Suma Babu, Sean M. Healey Center for ALS at MGH
Location and Time: Poster Session 2, Abstract:136, October 5, 2023, 4:30p - 6:30p ET
About OrphAI Therapeutics
OrphAI Therapeutics’ mission is to transform the lives of patients with rare diseases. The company is currently developing three investigational therapies across multiple orphan indications: AIT-101, a first-in-class PIKfyve inhibitor, which recently completed a Phase 2a clinical trial in amyotrophic lateral sclerosis (ALS); LAM-001, a proprietary inhaled form of rapamycin, currently in Phase 2 for bronchiolitis obliterans syndrome (BOS) and pulmonary arterial hypertension (PAH); and AIT-102, a proprietary analogue of mithramycin, in preclinical development for the treatment of SWI/SNF mutated or dysregulated tumors. To learn more, please visit: OrphAI-Therapeutics.com
MEDIA CONTACT:
info@orphai-therapeutics.com
For more details,please visit the original website
The content of the article does not represent any opinions of Synapse and its affiliated companies. If there is any copyright infringement or error, please contact us, and we will deal with it within 24 hours.
Organizations
-Drugs
Hot reports
Get started for free today!
Accelerate Strategic R&D decision making with Synapse, PatSnap’s AI-powered Connected Innovation Intelligence Platform Built for Life Sciences Professionals.
Start your data trial now!
Synapse data is also accessible to external entities via APIs or data packages. Leverages most recent intelligence information, enabling fullest potential.