Elixirgen Therapeutics Presents Preclinical Data with Bobcat mRNATM Technology in Duchenne Muscular Dystrophy at the 2024 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference
04 Mar 2024
mRNAsiRNAVaccine
Bobcat mRNATM technology is a novel linear mRNA platform able to encode large proteins
Data showed restoration of muscular function in DMD mouse model
BALTIMORE, March 04, 2024 (GLOBE NEWSWIRE) -- Elixirgen Therapeutics, Inc., a clinical-stage biotechnology company focused on the discovery, development and commercialization of therapies using its mRNA platforms, today presented preclinical data on its proprietary Bobcat mRNATM technology in a poster presentation at the 2024 Muscular Dystrophy Association (MDA) Clinical & Scientific Conference taking place March 3-6, 2024, in Orlando, Florida. Bobcat mRNATM is designed to deliver large protein payloads (over 13 kb), and results show that a Bobcat mRNATM encoding a full-length dystrophin protein can restore muscular function in a mouse model for Duchenne muscular dystrophy (DMD).
“We’re excited to be presenting these promising data on our novel Bobcat mRNATM technology. Dystrophin, the largest known human gene, is mutated in DMD, which is a rare disease that causes progressive muscle weakness and atrophy,” said Aki Ko, Co-Founder and Chief Executive Officer of Elixirgen Therapeutics. “Our Bobcat mRNATM full-length dystrophin approach may be complementary to others currently approved or in development, or may even mitigate some of their issues. We’re pleased to add the Bobcat mRNATM technology to our pipeline of RNA technologies and look forward to sharing updates in the months ahead.”
Presentation Title:Development of mRNA Therapeutic Delivering Full-length Dystrophin for Duchenne Muscular Dystrophy
Poster Number: T428
About Elixirgen Therapeutics, Inc.
Elixirgen Therapeutics, Inc. is a clinical-stage biotechnology company focused on the discovery, development and commercialization of therapies using its mRNA platforms and ZSCAN4 technology. The company has one ongoing (NCT04211714) and one completed (NCT04863131) Phase 1/2 clinical trial. For more information, visit ElixirgenTx.com.
Forward-Looking Statements
This press release may contain "forward-looking" statements. Actual results may differ materially from those set forth in this press release due to the risks and uncertainties inherent in pharmaceutical research and development. Any forward-looking statements in this press release speak only as of the date of this press release, and Elixirgen Therapeutics undertakes no obligation to update or revise the statements in the future, even if new information becomes available.
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LifeSci Communications
snissan@lifescicomms.com
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