Drug Type AAV based gene therapy |
Synonyms gamma-sarcoglycan gene-containing recombinant AAV1 vector based therapy (Genethon) |
Target- |
Action- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Muscular Dystrophies, Limb-Girdle | Phase 2 | France | 26 May 2008 |





