Last update 08 May 2025

scAAV5-GRK-HE

Overview

Basic Info

Drug Type
Gene editing
Synonyms
AAV5 rhodopsin gene therapy (Precision Biosciences/University of North Carolina)
Target
RP4
Action
modulators
Mechanism
RHO gene modulators(Rhodopsin gene modulators)
Therapeutic Areas
Congenital DisordersEye DiseasesOther Diseases
Active Indication
Retinitis Pigmentosa
Inactive Indication-
Originator Organization
Precision BioSciences, Inc.Precision BioSciences, Inc.
Active Organization
Precision BioSciences, Inc.Precision BioSciences, Inc.The University of North Carolina at Chapel HillThe University of North Carolina at Chapel Hill
Inactive Organization-
License Organization-
Drug Highest PhasePreclinical
First Approval Date-
Regulation-

Related

100 Clinical Results associated with scAAV5-GRK-HE
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100 Translational Medicine associated with scAAV5-GRK-HE
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100 Patents (Medical) associated with scAAV5-GRK-HE
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100 Deals associated with scAAV5-GRK-HE
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R&D Status

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IndicationHighest PhaseCountry/LocationOrganizationDate
Retinitis PigmentosaPreclinical
United States
Precision BioSciences, Inc.Precision BioSciences, Inc.
-
Retinitis PigmentosaPreclinical
United States
The University of North Carolina at Chapel HillThe University of North Carolina at Chapel Hill
-
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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