Last update 19 Sep 2024

Aceneuramic acid

Overview

Basic Info

Drug Type
Small molecule drug
Synonyms
Ace-ER, Aceneuramic acid (JAN/USAN), Kepnetic
+ [14]
Mechanism
sialic acid modulators
Inactive Indication
Originator Organization
Drug Highest PhaseApproved
First Approval Date
RegulationOrphan Drug (US)
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Structure

Molecular FormulaC11H19NO9
InChIKeyKBGAYAKRZNYFFG-BOHATCBPSA-N
CAS Registry131-48-6

External Link

R&D Status

Approved
10 top approved records.
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IndicationCountry/LocationOrganizationDate
Distal Myopathy, Nonaka Type
JP
-
Developing
10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Distal Myopathy, Nonaka TypeNDA/BLA
GB
20 May 2015
Distal Myopathy, Nonaka TypeNDA/BLA
FR
20 May 2015
Distal Myopathy, Nonaka TypeNDA/BLA
IL
20 May 2015
Distal Myopathy, Nonaka TypeNDA/BLA
US
20 May 2015
Distal Myopathy, Nonaka TypeNDA/BLA
IT
20 May 2015
Distal Myopathy, Nonaka TypeNDA/BLA
BG
20 May 2015
Distal Myopathy, Nonaka TypeNDA/BLA
CA
20 May 2015
ThrombocytopeniaDiscovery-01 Sep 2016
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date
Phase 3
89
(bmtxyeflim) = ompexcuaou zyahwgcqsc (inkcidyswa )
Negative
30 Apr 2019
Placebo
(bmtxyeflim) = ddrfogyphn zyahwgcqsc (inkcidyswa )
Phase 2
42
(UX001 6g/Day)
(jdnsvfckkg) = fjqyxqydpw yvyhqoiyyi (brxbpryqbz, nnyhgrhkza - jyfmtdpkfg)
-
19 Feb 2019
(Ace-ER 6 g/Day)
brutixsnut(fvyepnlurp) = cyoxdpkicb zcyzyghxxo (zmtbrbotxp, ncbmqyvuww - aowawkndfx)
Phase 3
89
Placebo
spbswxlojm(tvqphpafnd) = tuvivqdwye brhucfufbe (usippvpufw, qnidqizbwj - gsqfpumdgx)
-
09 Jul 2018
Phase 2
59
(Crossover Participants)
olvatsovsp(cwcrawcyhi) = kxdeshfjdb hjxkwwafkt (ucigmptbie, egwvqephcj - nauhnjcufx)
-
13 Mar 2018
(Naïve Participants)
mdwyqlrzht(oguvyswzfl) = hdzqslmrhz nokddutixg (cgzmebrsgr, uzivvfhddd - icydxmgxej)
Phase 2
30
(ywmurxdruk) = snxwvagpff ebjyugqoii (lgkvtskzmq )
-
15 Jul 2004
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Regulation

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